Spain
Fundació Hospital Universitari Vall d’Hebron- Institut de Recerca (VHIR)
Barcelona, Spain
Coordinating investigator: Dr. Pere Soler Palacin
Contact: miriam.gonzalezamores@vallhebron.cat
Poland
Wroclaw Medical University, Department of Pediatric Hematology/Oncology and BMT Supraregional Center of Pediatric Oncology "Cape of Hope"
Wroclaw, Poland
Coordinating investigator: Prof. Dr. Krysztof Kalwak
Contact: krzysztof.kalwak@gmail.com, koh@usk.wroc.pl
United Kingdom
University College London Great Ormond Street Institute of Child Health (UCL GOSH)
London, UK
Coordinating investigator: Dr. Claire Booth
Contact: Claire Booth: Claire.Booth@gosh.nhs.uk/ Agnieszka Kubat: a.kubat@ucl.ac.uk:
Turkey
Erciyes Üniversitesi TIP Fakültesi Pediatrik Hemtoloji Onkoloji BD Erciyes Pediatrik Kemik iligi Nakli Merkezi
Keyseri, Turkey
Coordinating Investigator: Prof. Dr. Musa Karakükcü
Contact: erpedkit@gmail.com
Australia
The Royal Children's Hospital
Melbourne, Victoria, Australia
Coordinating Investigator: A/Prof Rachel Conyers & A/Prof Theresa Cole
Contact:genetherapy@rch.org.au/ Rachel.conyers@rch.org.au / Theresa.cole@rch.org.au